uniQure is delivering on the promise of gene therapy – single treatments with potentially curative results. We are leveraging our modular and validated technology platform to rapidly advance a pipeline of proprietary and partnered gene therapies to treat patients with hemophilia, Huntington’s disease and other severe genetic diseases.
We are advancing a focused pipeline of innovative gene therapies. We are currently conducting a pivotal phase 3 trial in our lead indication, hemophilia B, and will initiate a Phase I/II trial in Huntington’s disease in the second half of 2019. Our pipeline of adeno-associated virus (AAV)-based gene therapies has been developed using an innovative technology platform, supported by industry-leading proprietary commercial-grade manufacturing capabilities.
Amsterdamse Science & Innovation Awards 2021 voor digitale urineweegschaal, nanofolie en dyslexiespel voor kinderen In NEMO Amsterdam zijn voor de 15e keer de jaarlijkse Innovation Awards uitgereikt. De innovatieprijzen zijn een initiatief van de Innovation Exchange Amsterdam (IXA). IXA bekroont met de Awards vernieuwende ideeën om de samenleving te verbeteren van jonge wetenschappers, allemaal verbonden […]
NewsHalleh Ghorashi, Jeroen Kluck and Hergen Spits winners Impact Award 2021!
NewsHalleh Ghorashi, Jeroen Kluck en Hergen Spits winnaars Impact Award 2021!
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